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filingDate 2006-04-20-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_84397d1f9782b74bbff633c273409450
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publicationDate 2007-11-01-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2007123391-A1
titleOfInvention Therapeutic intervention in a genetic disease in an individual by modifying expression of an aberrantly expressed gene.
abstract The present invention provides means and methods for alleviating genetic disease. A genetic defect that has a phenotype in differentiated cells can lead to defects in precursor cells thereof. These so-called secondary defects contribute to the overall disease of the individual. In the present invention, genetic intervention with the aim to alleviate symptoms of genetic disease is directed toward the primary genetic defect in the differentiated cell and the secondary defect in the precursor cell.
priorityDate 2006-04-20-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA0A2I7G3B0
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID6892
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP04414
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID21803
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID678759
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID296197
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCF1R741
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP16858
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6J1J2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5XJ10
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID407216
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP11532
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00563
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCF1R0H8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6JV22
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP11530
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ59800
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4217
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ59906
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5XLD3
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID16009
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP35834
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID558212
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4792
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP11533
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID23052
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8UWD9
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID432140
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP35833
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID652
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8UWD8
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID154467
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID45124501
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID398071
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCF1PKH2
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID533861
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID517812
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID56940027
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP17329
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8UWE0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCF1PI70
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID335821
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID84182
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP09124
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID395097
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID6886
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID56473
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID480454
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID52538
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID62693680
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID13856
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4344564
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID419815
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID397249
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID281096
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5XDW3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCF1NNP2
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID5953295
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID13346
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID16002
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB6YUU0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP14202
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID114495
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6H8T0
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID21678
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID301509
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4175
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID549693
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID60374
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6H8S9
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID406188
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID66578660
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID462158
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ7M303
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID403420
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID260321
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6H8T2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA3CYG8
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100034367
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID56431
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID25317
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCE2RJ14
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO02708
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100171813
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6H8T1
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID373313
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP11052
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID6640
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP03969
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68197
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8UWD7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP13863
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID58078
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID282653
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID395030
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID45539638
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ86XR8
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID57208107
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ59309
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID821
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID54250
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID42591
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ865V0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC4KHW5
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID39266
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID480124
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID45716361
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID533136
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP34556
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID421718
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP27730
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5R440
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8CEE0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ2XNF5
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID17700
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5IGQ0
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID20595
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID424295
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP42706
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP27726
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP42705
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07335
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5IS69
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID369197
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9I7S9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCK7GS36
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID548975
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID445474
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID563799
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID480291
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID41392067
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID414859283

Total number of triples: 1124.