Predicate |
Object |
assignee |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_a873373fda6093ddbc0d06d039612dc4 |
classificationCPCAdditional |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-11 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-351 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-3513 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-321 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-3233 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2320-31 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2320-35 |
classificationCPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K31-7088 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P21-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-113 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-115 |
classificationIPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C07H21-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K31-7088 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-115 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-113 |
filingDate |
2013-10-04-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
grantDate |
2016-01-26-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
inventor |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_f636e8ac977e85de524a9901d0963317 http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_27dac9010c0a3e74c73ccdde2f059d1c http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_8754c45143892a43fa0365a6242d618b |
publicationDate |
2016-01-26-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
publicationNumber |
US-9243252-B2 |
titleOfInvention |
Oligomers |
abstract |
Molecules are provided for inducing or facilitating exon skipping in forming spliced mRNA products from pre-mRNA molecules in cells. The molecules may be provided directly as oligonucleotides or expression products of vectors that are administered to a subject. High rates of skipping can be achieved. High rates of skipping reduce the severity of a disease like Duchene Muscular Dystrophy so that the disease is more like Becker Muscular Dystrophy. This is a severe reduction in symptom severity and mortality. |
isCitedBy |
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10881743-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10787519-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11142767-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11253607-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11555190-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11246941-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11179472-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11497814-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11311627-B1 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11525137-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11576980-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11712478-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11583591-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10457944-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11697811-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10994020-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2018129384-A1 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11400163-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-9970010-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11554176-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10800848-B2 |
priorityDate |
2008-09-11-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
type |
http://data.epo.org/linked-data/def/patent/Publication |