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filingDate 2011-06-27-04:00^^<http://www.w3.org/2001/XMLSchema#date>
grantDate 2016-01-26-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_78c592e3c1c5376c6f455883b7e121e0
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_f55a7086be7f3dd24202696f51987430
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publicationDate 2016-01-26-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-9241929-B2
titleOfInvention Prophylactic or ameliorating agent for genetic diseases
abstract An object of the present invention is to provide a prophylactic or ameliorating agent for a genetic disease that is caused by a mutation in an exon of a gene and is capable of forming a functional truncated protein by skipping of the exon comprising the mutation. The prophylactic or ameliorating agent used in the present invention is a prophylactic or ameliorating agent for a genetic disease that is caused by a mutation in an exon of a gene and is capable of forming a functional truncated protein by skipping of the exon comprising the mutation, wherein the prophylactic or ameliorating agent contains a compound having a molecular weight of 1500 or lower.
priorityDate 2010-06-28-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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