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publicationDate 2015-10-13-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-9157120-B2
titleOfInvention Methods and compositions for the treatment of huntington's disease
abstract Methods and compositions for reducing expression of a mutant huntingtin (mHTT) protein in a cell are provided. Such methods include contacting the cell with an effective amount of a nucleic acid silencing agent targeting a differentiating polymorphism in RNA encoding the mHTT.
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