http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-2023022146-A1

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filingDate 2020-06-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_7540a5580a2b3f27a49ca9c18e97fdd8
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_acccf1a6348f186f412cdf05e37c29b6
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http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_ca361803858a285f772aa07ed1c238ca
publicationDate 2023-01-26-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2023022146-A1
titleOfInvention Compositions and methods for editing beta-globin for treatment of hemaglobinopathies
abstract The disclosure features methods of correcting a mutation in the human beta-globin (HBB) gene in a cell or population of cells. The disclosure also features methods of increasing repair of a DNA double stranded break (DSB) in an HBB gene by the homology-directed repair (HDR) pathway. The disclosure also features compositions for use in the methods.
priorityDate 2019-06-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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Total number of triples: 1798.