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filingDate 2022-06-02-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2022-12-08-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2022387627-A1
titleOfInvention Vectors and gene therapy for treating cornelia de lange syndrome
abstract The present disclosure relates to AAV gene therapy vectors, AAV replicons, and pharmaceutical compositions for delivering a human HDAC8 gene to a subject for treating Cornelia de Lange Syndrome. In addition, methods of treatment and gene transfer are provided.
priorityDate 2021-06-03-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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