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filingDate 2022-04-18-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2022-10-13-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2022325280-A1
titleOfInvention Antisense oligonucleotides and their use for treating pendred syndrome
abstract The present disclosure relates to the field of medicine. In particular, it relates to novel antisense oligonucleotides that prevent or reduce exon 8 skipping in the SLC26A4 gene during pre-mRNA splicing, and their use in the treatment of Pendred Syndrome.
priorityDate 2020-02-12-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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