http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-2022213478-A1

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classificationCPCInventive http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-111
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filingDate 2020-04-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_137b42a558ce6fb77188a7db2a6e5d96
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_626462bd042501164dffdcbabd5dba06
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publicationDate 2022-07-07-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2022213478-A1
titleOfInvention Antisense oligonucleotides for the treatment of usher syndrome
abstract The invention relates to the fields of medicine. In particular, it relates to novel antisense oligonucleotides (AONs) that are capable of skipping exon 62 from human USH2A premRNA and that may be used in the treatment, prevention and/or delay of Usher syndrome type II and/or USH2A-associated non syndromic retina degeneration.
priorityDate 2019-04-18-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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