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filingDate 2019-06-27-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_f79d2b13749497971d1e094a2d59f092
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publicationDate 2021-09-02-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2021269829-A1
titleOfInvention Optimized cln5 genes and expression cassettes and their use
abstract This invention relates to polynucleotides comprising optimized CLNS open reading frame (ORF) sequences, vectors comprising the same, and methods of using the same for delivery of the ORF to a cell or a subject and to treat disorders associated with aberrant expression of a CLNS gene or aberrant activity of a CLNS gene product in the subject, such as CLNS disease.
priorityDate 2018-06-28-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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