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filingDate 2020-12-31-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_aa7a0ea9bcc66a22b888dcac5af1fbf7
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_3183fd923af2857b23ca3012469c4524
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publicationDate 2021-05-20-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2021145906-A1
titleOfInvention Compositions and methods for treating diseases
abstract The present invention provides compositions and methods of use pertaining to rAAV-mediated delivery of therapeutically effective molecules for treatment of diseases such as Pompe disease. These compositions in combination with various routes and methods of administration result in targeted expression of therapeutic molecules in specific organs, tissues and cells.
priorityDate 2007-02-23-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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