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filingDate 2019-08-09-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_dfedebd4eef53c209d6cc5fa3b620e00
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_8643b91b06f9b668f8a19a8a68763208
publicationDate 2020-07-09-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2020216846-A1
titleOfInvention Antisense Compounds and Uses Thereof
abstract The present invention provides compounds comprising oligonucleotides complementary to a CLN3 transcript. Certain such compounds are useful for hybridizing to a CLN3 transcript, including but not limited to a CLN3 transcript in a cell. In certain embodiments, such hybridization results in modulation of splicing of the CLN3 transcript. In certain embodiments, such compounds are used to treat one or more symptoms associated with Batten Disease.
priorityDate 2013-12-02-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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