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filingDate 2019-07-10-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2020-06-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2020181613-A1
titleOfInvention Compositions and methods for modulation of smn2 splicing
abstract Disclosed herein are compounds, compositions and methods for modulating splicing of SMN2 mRNA in a cell, tissue or animal. Also provided are uses of disclosed compounds and compositions in the manufacture of a medicament for treatment of diseases and disorders, including spinal muscular atrophy.
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