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publicationDate 2019-11-14-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2019343966-A1
titleOfInvention Gene therapy for treating hemophilia a
abstract Compositions and regimens useful in treating hemophilia A are provided. The compositions include recombinant adeno-associated virus (rAAV) with a transthyretin enhancer and promoter driving expression of a human Factor VIII.
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