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inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_539fd45554fb14da04e6d78fc59479af
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publicationDate 2019-10-31-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2019330626-A1
titleOfInvention Compounds and methods for use in dystrophin transcript
abstract Provided herein are methods, compounds, and compositions for modulation of dystrophin pre-mRNA in an animal. Such methods, compounds, and compositions are useful, for example, to treat, prevent, or ameliorate one or more symptoms of Duchenne Muscular Dystrophy disease.
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Total number of triples: 426.