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filingDate 2017-07-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_4e9b7b79755788d63514b1d00d37a207
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publicationDate 2019-10-24-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2019323006-A1
titleOfInvention Compounds and methods for modulation of smn2
abstract Disclosed herein are compounds, compositions and methods for modulating splicing of SMN2. Also provided are uses of disclosed compounds and compositions in the manufacture of a medicament for treatment of spinal muscular atrophy.
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Total number of triples: 423.