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publicationDate 2019-08-29-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2019264210-A1
titleOfInvention Compound and method for treating myotonic dystrophy
abstract Provided are 9-base morpholino antisense compounds targeted to polyCUG repeats in the 3′UTR region of dystrophia myotonica protein kinase (DMPK) mRNA, and related methods for treating myotonic dystrophy DM1.
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