http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-2018169269-A1

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filingDate 2016-05-31-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_114bd6c122efb3fa55d33ed5f9583e3d
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publicationDate 2018-06-21-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2018169269-A1
titleOfInvention Methods of delivery of transgenes for treating brain diseases
abstract The present disclosure provides methods of treating a disease or delivering a therapeutic agent to a mammal comprising administering to the mammal's deep cerebella nuclei a recombinant adeno-associated virus (rAAV) particle comprising an AAV capsid protein and a vector comprising a nucleic acid encoding a therapeutic agent inserted between a pair of AAV inverted terminal repeats in a manner effective to infect the CNS cell of the non-rodent mammal such that the CNS cell expresses the therapeutic agent in the non-rodent mammal.
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID453
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ28513
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP14972
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4336216
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID135398635
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP10618
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6JV22
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ06657
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP11212
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100049397
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100002479
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID11757
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ01558
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP53361
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419552372
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9QL89
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226395183
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ66T65
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ63540
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP11211
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ0Z956
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID32545
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCF5CPE8
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226395182
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ59309
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226393946
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP13393
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP27260
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO34425
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8PTD3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DMD5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA4PBT0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP81558
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID24547
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4155
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9U568
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID326270
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP57384
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9INJ1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ01651
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB1YD06
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA6UUN9
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2597
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0C570
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO88780
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226399605
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ55031
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP9WN83
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9JGU1
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID402874
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ86523
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02688
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP9WN82
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID75038
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO14746
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID565841
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02687
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCJ9PAA7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ971V3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP39460
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP83487
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID23961
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9IB50
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA6URW1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ2XNF5

Total number of triples: 707.