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filingDate 2016-04-26-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_f6860f0b5d44b5f6198bc890ca5a2a4b
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publicationDate 2018-04-26-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2018110877-A1
titleOfInvention DUAL AAV VECTOR SYSTEM FOR CRISPR/Cas9 MEDIATED CORRECTION OF HUMAN DISEASE
abstract A dual vector expression system is provided for delivery of CRISPR/Cas9, sgRNA and donor templates for supplying corrected genes or gene sequences to neonatal subjects. An AAV8 system for delivery to proliferating cells such as hepatocytes is described, as are other dual AAV vector systems for targeting to other cells.
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID15764346
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP13234
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP03252
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6BZ43
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9ESV6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5E7B6
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID41247
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100682528
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID37888
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP08414
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB6JWC1
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID853
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID465887
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP51009
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB6QS64
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ96629
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP11798
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID5280352
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA4YHA5
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226393895
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID23830
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID280989
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0AC86
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9HSS7
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID485769
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID912048
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID2725057
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6D8H5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0AC87
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID19161
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID9793
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID7175
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID272636
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID101453374
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226393858
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP27726
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5V061
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA5DA88
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO04879
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8FCR9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ20EU8
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100009074
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ96NX5
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID41183
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9HJ69
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5RA72
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO52631
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0A100
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID380259
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID473838
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00356
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP30202
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8PTD3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00355
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ01651
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100538330
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA6VDY0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00362
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00361
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID38423
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ58546
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0A0Z9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP03253
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB0BNY0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB5X4Z4
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO50258
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1786
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9YGI5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA3N062
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID6853
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID396101
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO40958
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ59906
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB7LW98
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID3423
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID84350
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID57122066
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ59800
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9TXJ0
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID331535
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ1KVQ9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP55971
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO59841
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9YFS9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB5FAS8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO59494
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA5DWN5
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID368517
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226410796
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP48677
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP9WMW1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP11937
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA1DH62
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID779340
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID31527606
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID368516
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP9WMW0

Total number of triples: 733.