http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-2017268000-A1

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classificationCPCInventive http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K31-7088
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classificationIPCInventive http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-113
filingDate 2014-12-02-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_cf0d135a9cd2d009a3d324a87149d48c
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_e335ccaf856fddf5e698e4c0d4faae00
publicationDate 2017-09-21-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2017268000-A1
titleOfInvention Antisense compounds and uses thereof
abstract The present invention provides compounds comprising oligonucleotides complementary to a CLN3 transcript. Certain such compounds are useful for hybridizing to a CLN3 transcript, including but not limited to a CLN3 transcript in a cell. In certain embodiments, such hybridization results in modulation of splicing of the CLN3 transcript. In certain embodiments, such compounds are used to treat one or more symptoms associated with Batten Disease.
isCitedBy http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2020055917-A1
priorityDate 2013-12-02-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID4781
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226399566
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID415822905
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID455485704
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID227098489
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID58260126
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID66586650
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID70751
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID420238481
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419510188
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID122948
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID166734
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID58260125
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226417276
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID453
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID720471

Total number of triples: 323.