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publicationDate 2016-10-20-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2016304854-A1
titleOfInvention Mitochondrial genome editing
abstract Methods of preventing the transmission of a mitochondrial disease, disorder, or condition using mitochondria-targeted enzymes or mRNA encoding mitochondria-targeted enzymes. The methods as described herein can specifically eliminate mitochondrial DNA (mtDNA) mutations in the germline.
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