Predicate |
Object |
assignee |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_d77666cadbbfb580dcf6af28e3db45e4 |
classificationCPCAdditional |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-321 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-315 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-11 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2320-33 |
classificationCPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12Y302-0102 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-111 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-1137 |
classificationIPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-113 |
filingDate |
2014-09-10-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
inventor |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_b947b27ae56dcfce7f13aebb5b272f41 http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_f72a336383120bf9fcdeab6531d126c5 |
publicationDate |
2016-07-28-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
publicationNumber |
US-2016215291-A1 |
titleOfInvention |
Nucleic acids and methods for the treatment of pompe disease |
abstract |
The invention relates to nucleic acids and methods for restoring acid alpha-glucosidase (GAA) activity in patients with Pompe disease using splice-switching technology. |
isCitedBy |
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10696969-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11083745-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10538764-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10913947-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10941405-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11096956-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10683503-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11702660-B2 |
priorityDate |
2013-09-11-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
type |
http://data.epo.org/linked-data/def/patent/Publication |