http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-2016051638-A1

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filingDate 2015-09-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2016-02-25-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2016051638-A1
titleOfInvention Methods for treating lysosomal acid lipase deficiency in patients
abstract The present invention provides methods of treating LAL deficiency comprising administering to a mammal a therapeutically effective amount of lysosomal acid lipase with an effective dosage frequency. Methods of improving growth and liver function, increasing LAL tissue concentration, and increasing LAL activity in a human patient suffering from LAL deficiency are also provided.
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Total number of triples: 917.