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filingDate 2014-12-29-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_39f526784f02fd42f175df02f93dac9d
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publicationDate 2015-12-10-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2015353929-A1
titleOfInvention Compositions and methods for modulation of smn2 splicing
abstract Disclosed herein are compounds, compositions and methods for modulating splicing of SMN2 mRNA in a cell, tissue or animal. Also provided are uses of disclosed compounds and compositions in the manufacture of a medicament for treatment of diseases and disorders, including spinal muscular atrophy.
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