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filingDate 2013-06-06-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_2c5a62fa78988162878c442d7e2f3f48
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publicationDate 2015-05-28-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2015147309-A1
titleOfInvention Allosteric chaperones and uses thereof
abstract The present invention relates to an allosteric non-inhibitory chaperone of the lysosomal acid alpha-glucosidase (GAA) for use in the treatment of a pathological condition characterized by a deficiency of the lysosomal acid alpha-glucosidase (GAA), to pharmaceutical composition thereof, to a method for increasing the activity of GAA in a subject and to a method for identifying an allosteric non-inhibitory chaperone for GAA.
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