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inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_8733f2b57daf1ce6b2968f0cd69081ac
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publicationDate 2014-12-04-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2014357698-A1
titleOfInvention Modulation of exon recognition in pre-mrna by interfering with the secondary rna structure
abstract The invention relates to oligonucleotides for inducing skipping of exon 53 of the dystrophin gene. The invention also relates to methods of inducing exon 53 skipping using the oligonucleotides.
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