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filingDate 2011-10-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_2ab3c6a4ec3c6a0f37de23458395dd19
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publicationDate 2012-07-12-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2012177605-A1
titleOfInvention Delivery of Polynucleotides Across the Blood-Brain-Barrier Using Recombinant AAV9
abstract The present invention relates to methods and materials useful for systemically delivering polynucleotides to the spinal cord. Use of the methods and materials is indicated, for example, for treatment of lower motor neuron diseases such as spinal muscular atrophy (SMA) and amyotrophic lateral sclerosis (ALS) as well as Pompe disease and lysosomal storage disorders.
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID558154
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ27957
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCE1BCL0
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ06AV0
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCF1SBT4
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6GUL6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP18109
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP21674
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP18254
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA0A6I8RCQ3
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ90322
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ16625
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9I9M2
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID56419127
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCD3ZQL7
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO61608
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9JKD6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP21948
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID78405
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ2HJ22
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO62650
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID7422
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC0K3N5
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID16000
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100125267
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA0A1I7Q421
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Total number of triples: 888.