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publicationDate 2011-05-05-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-2011104727-A1
titleOfInvention Assays for diagnosing and evaluating treatment options for fabry disease
abstract Provided are in vitro and in vivo methods for determining whether a patient with Fabry disease will respond to treatment with a specific pharmacological chaperone.
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