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publicationNumber US-2010330052-A1
titleOfInvention Use of Mesenchymal Stem Cells for Treating Genetic Diseases and Disorders
abstract A method of treating a genetic disease or disorder such as, for example, cystic fibrosis, Wilson's disease, amyotrophic lateral sclerosis, or polycystic kidney disease, in an animal comprising administering to said animal mesenchymal stem cells in an amount effective to treat the genetic disease or disorder in the animal.
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