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filingDate 2019-05-28-04:00^^<http://www.w3.org/2001/XMLSchema#date>
grantDate 2022-08-23-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2022-08-23-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-11421219-B2
titleOfInvention Methods and compositions for treating Leber congenital amaurosis
abstract Expression vectors, viral particles and therapeutic methods of using such constructs to improve the visual function of a patient suffering from diseases of the eye, resulting from failure to produce a specific protein in the eye, or the production of a non-functional protein in the eye, particularly Leber Congenital Amaurosis (LCA) and CEP290-related LCA.
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