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inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_2bc03041cdba45e25fe7ca6407421c13
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publicationDate 2021-12-14-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-11198858-B2
titleOfInvention Codon optimized GLA genes and uses thereof
abstract The present disclosure provides codon optimized nucleotide sequences encoding human alpha-galactosidase A, vectors, and host cells comprising codon optimized alpha-galactosidase A sequences, and methods of treating disorders such as Fabry disease comprising administering to the subject a codon optimized sequence encoding human alpha-galactosidase A.
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