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filingDate 2019-06-04-04:00^^<http://www.w3.org/2001/XMLSchema#date>
grantDate 2021-03-02-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_e4405bc6e9785b364564777943e80108
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publicationDate 2021-03-02-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-10933083-B2
titleOfInvention Hydroxypropyl beta-cyclodextrin compositions and methods
abstract This disclosure provides mixtures of beta-cyclodextrin molecules substituted at one or more hydroxyl positions by hydroxypropyl groups, the mixture optionally including unsubstituted beta-cyclodextrin molecules, for use as a pharmaceutically active ingredient; methods of making such mixtures; methods of qualifying such mixtures for use in a pharmaceutical composition suitable for intrathecal or intracerebroventricular administration; pharmaceutical compositions suitable for intrathecal or intracerebroventricular administration comprising such mixtures; and methods of using the pharmaceutical compositions for treatment of Niemann-Pick disease Type C.
priorityDate 2015-06-10-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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Total number of triples: 611.