abstract |
The present invention provides a protein function regulator for restoring protein homeostasis, including GSPT1 activity. The invention provides methods for modulating protein-mediated diseases, such as GSPT1-mediated diseases, disorders, conditions, or responses. Compositions are also provided. Methods of treating, ameliorating, or preventing protein-mediated diseases, disorders, and conditions are also provided, such as GSPT1-mediated diseases, disorders, and conditions, including cancer and astrocyte proliferation. |