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filingDate 2019-07-26-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2021-04-14-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber KR-20210040984-A
titleOfInvention Treatment of mycopolysaccharide IVA
abstract Herein, mucopolysaccharide type IVA (MPS) involves the use of a recombinant adeno-associated virus (rAAV) to deliver human N-acetylgalactosamine-6-sulfate sulfatase (hGALNS) to the bones of a human subject diagnosed with MPS IVA. IVA). Also provided herein are rAAVs that can be used in gene therapy and methods of making such rAAVs.
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Total number of triples: 950.