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filingDate 2018-10-19-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_d0a1665faa9f872c4b3d0867eed401f1
publicationDate 2020-07-08-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber KR-20200083495-A
titleOfInvention Methods and materials for NT-3 gene therapy
abstract The present invention relates to the delivery of recombinant adeno-associated virus (rAAV) of neurotrophin 3 (NT-3) polynucleotides. The present invention provides methods of using rAAV and rAAV for NT-3 gene therapy to improve muscle strength, stimulate muscle growth, and treat muscle wasting disorders such as muscular dystrophy and Sharko-Marie-Tooth neuropathy.
priorityDate 2017-10-20-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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Total number of triples: 1194.