http://rdf.ncbi.nlm.nih.gov/pubchem/patent/KR-20160029615-A

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filingDate 2014-11-20-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_a63bea708a9a798cdefa66d8ec0666a6
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_37966862a361745f941fe737b252526f
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_9278f274a5d6a03a3f6b295792758373
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_0ac3bda986406328cc655d4272927c9d
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_bc6b6ef01967c53cd8e43b8b9bb6bc56
publicationDate 2016-03-15-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber KR-20160029615-A
titleOfInvention GM1 gangliosidosis human cell model and use thereof
abstract The present invention relates to a method for producing a model cell based on a human cell model of GM1 gangliosidosis, induced pluripotent stem cells (iPSCs) and iPSCs-derived neural progenitor cells, IPSCs derived from a fibroblast of a GM1 patient of the present invention are useful as a neural progenitor cell (NPC) and a neural progenitor cell And the cells can differentiate into GM1 gangliosides and lysosomes, which are symptoms of GM1, as a model cell of GM1. Therefore, it is possible to identify the GM1 pathogenesis mechanism analysis study and therapeutic agent It can be useful for research for development. Also, it was confirmed that rhIL1RA or Z-YVAD-FMK, which is an inflammation-regulating complex inhibitor, could be used as a symptomatic remedy / remedy for GM1 gangliosidosis by using the GM1 cell model of the present invention.
priorityDate 2014-09-05-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP23989
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP45582
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP77989
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8A9Q8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCF7B044
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9PJN6
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID561924
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC3NGT6
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID7009644
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO01382
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8A934
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID13346
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID97364
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8A6V8
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID10376
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID426383963
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID405770
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO32755
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID415818685
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC3NEV8
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID282857
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100859104
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID415974143
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP37840
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP57384
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID168058
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8A4C3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO62654
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID7009598
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8A3N2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8PTD3
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID426383892
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID399342
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ7MG04

Total number of triples: 663.