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filingDate 2020-02-04-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationDate 2022-03-24-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber JP-2022519596-A
titleOfInvention Adeno-associated virus delivery of CLN3 polynucleotide
abstract The present disclosure relates to recombinant adeno-associated virus (rAAV) delivery of a celloid lipofuscinosis neuron 3 (CLN3) polynucleotide. The present disclosure provides methods of using rAAV and rAAV for the treatment of the CLN3 gene for neuronal ceroid lipofuscinosis or CLN3-Batten disease. [Selection diagram] None
priorityDate 2019-02-04-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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