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filingDate 2019-11-05-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationDate 2022-01-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber JP-2022506066-A
titleOfInvention Optimized FIG4 genes and expression cassettes and their use
abstract The present invention presents a polynucleotide containing an optimized FIG4 open reading frame (ORF) sequence, a vector containing it, and an abnormality of the FIG4 gene for delivery of the ORF to a cell or subject and in the subject. It relates to a disorder associated with expression or aberrant activity of the FIG4 gene product, such as its use for treating CMT4J. [Selection diagram] Fig. 1
priorityDate 2018-11-05-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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