abstract |
PROBLEM TO BE SOLVED: To treat lysosomal storage diseases such as Fabry disease, Pompe disease, Niemann-Pick A disease, Niemann-Pick B disease, Mucopolysaccharidosis type I, Mucopolysaccharidosis type II, and Mucopolysaccharidosis type VI. Provided is a pharmaceutical composition. The following: A compound having the structure of. [Selection diagram] Fig. 1 |