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filingDate 2017-07-05-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationDate 2019-08-22-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber JP-2019522972-A
titleOfInvention Pre-mRNA splice switching or regulatory oligonucleotides containing bicyclic scaffold moieties with improved characteristics for the treatment of genetic disorders
abstract The present invention provides antisense splice switching oligonucleotides with improved features that enhance clinical applicability to treat, ameliorate, prevent and / or delay neuromuscular disorders such as DMD. [Selection figure] None
priorityDate 2016-07-05-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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Total number of triples: 899.