abstract |
An object of the present invention is to provide a method for treating Pompe disease. The above problem has been solved by providing a method for treating Pompe disease using human acid α-glucosidase. A preferred treatment regime includes administering more than 10 mg / kg body weight per week to the patient. Administration is preferably intravenous. This method can be used for the treatment of patients with infantile, juvenile or adult Pompe disease. The human acid alpha glucosidase is preferably obtained in the milk of a non-human transgenic mammal and is preferably predominantly in the form of 110 kD. [Selection figure] None |