Predicate |
Object |
classificationCPCAdditional |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2320-30 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-33 |
classificationCPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K9-0019 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P1-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K31-7125 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P21-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P21-02 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-113 |
classificationIPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K48-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K31-7088 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61P21-02 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K31-573 |
filingDate |
2014-03-14-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
publicationDate |
2016-06-02-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
publicationNumber |
JP-2016516066-A |
titleOfInvention |
Improved composition for treating muscular dystrophy |
abstract |
An improved composition and method for treating muscular dystrophy by administering eteprilsen, an antisense molecule that can bind to selected target sites in the human dystrophin gene that induce exon skipping is described. In one aspect, a method is provided for treating Duchenne muscular dystrophy in a patient in need of treatment for Duchenne muscular dystrophy, comprising administering to the patient a dose of about 30 mg / kg eteprilsen once a week. including. |
isCitedBy |
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/JP-2018126160-A http://rdf.ncbi.nlm.nih.gov/pubchem/patent/JP-7125940-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11382981-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/JP-2020503010-A http://rdf.ncbi.nlm.nih.gov/pubchem/patent/JP-7118063-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/JP-2016517279-A http://rdf.ncbi.nlm.nih.gov/pubchem/patent/JP-2020503009-A |
priorityDate |
2013-03-15-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
type |
http://data.epo.org/linked-data/def/patent/Publication |