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filingDate 2014-03-14-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationDate 2016-06-02-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber JP-2016516066-A
titleOfInvention Improved composition for treating muscular dystrophy
abstract An improved composition and method for treating muscular dystrophy by administering eteprilsen, an antisense molecule that can bind to selected target sites in the human dystrophin gene that induce exon skipping is described. In one aspect, a method is provided for treating Duchenne muscular dystrophy in a patient in need of treatment for Duchenne muscular dystrophy, comprising administering to the patient a dose of about 30 mg / kg eteprilsen once a week. including.
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