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filingDate 2013-01-03-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationDate 2015-02-05-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber JP-2015503924-A
titleOfInvention Methods and compositions for gene transfer
abstract Disclosed herein is an AAV-based viral vector encoding GNE from muscle-specific and non-muscle-specific promoters, and its use in treating myopathy associated with altered GNE function. is there. [Selection] Figure 1
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