Predicate |
Object |
classificationCPCAdditional |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-331 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-11 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-14 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-315 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-321 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-346 |
classificationCPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-113 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P43-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P21-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P21-02 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P25-14 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P25-00 |
classificationIPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K31-7088 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N5-10 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61P21-02 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61P25-14 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K48-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12Q1-68 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12Q1-02 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-09 |
filingDate |
2009-02-05-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
publicationDate |
2011-04-07-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
publicationNumber |
JP-2011510678-A |
titleOfInvention |
Methods and means for treating DNA repeat instability related genetic disorders |
abstract |
The present invention contains bases capable of forming inosine and / or uracil and / or wobble base pairs for the manufacture of a medicament for diagnosis, treatment or prevention of genetic disorders associated with cis element repeat instability in humans A method of using said oligonucleotide, wherein said oligonucleotide is preferably substantially ribonuclease H-independent and complementary only to repetitive sequences in human gene transcripts, and Provide drugs. Accordingly, the present invention provides a method of treatment for cis-element repeat instability related genetic disorders. The invention also relates to modified oligonucleotides that can be used in the methods of the invention to prevent the accumulation and / or translation of repetitive extension transcripts in cells. |
isCitedBy |
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/JP-2020182472-A http://rdf.ncbi.nlm.nih.gov/pubchem/patent/JP-2018533975-A http://rdf.ncbi.nlm.nih.gov/pubchem/patent/JP-2015536301-A http://rdf.ncbi.nlm.nih.gov/pubchem/patent/JP-7089763-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/JP-2014513946-A http://rdf.ncbi.nlm.nih.gov/pubchem/patent/JP-2018027080-A http://rdf.ncbi.nlm.nih.gov/pubchem/patent/JP-2015514418-A |
priorityDate |
2008-02-08-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
type |
http://data.epo.org/linked-data/def/patent/Publication |