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filingDate 2008-05-23-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2009-06-25-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber JP-2009137933-A
titleOfInvention How to treat Gaucher disease
abstract Disclosed is a drug and a therapeutic method for treating late-onset Gaucher disease. Ambroxol, bromhexine, or a derivative thereof having activity as a pharmacological chaperone of a mutant of β-glucocerebrosidase. Therapeutic methods provide a therapeutically effective amount of the composition to a patient in need of treatment. [Selection figure] None
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