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publicationDate 2007-05-24-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber JP-2007513188-A
titleOfInvention Compositions and methods for the treatment of lysosomal storage diseases
abstract The present invention relates to a method of providing a lysosomal enzyme to a subject by administering a stem cell, preferably a pluripotent adult progenitor cell (MAPC). The present invention further relates to a method for treating lysosomal storage diseases by administering stem cells. The present invention also relates to a method for modulating the accumulation of a substrate in a subject comprising providing the subject with an effective amount of a lysosomal enzyme. The stem cells are Oct-3 / 4 positive and can give rise to endoderm, ectoderm and mesoderm cells and provide lysosomal enzymes.
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID533357
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID45875
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6D736

Total number of triples: 1630.