abstract |
An isolated antisense oligonucleotide (AON) selected from the group consisting of oligonucleotides having a sequence as set forth in SEQ ID NOs: 4-9, 11, 12, 14-29, and 31-34, wherein the antisense oligonucleotide specifically hybridizes to a target region of the exon of a γ-sarcoglycan RNA. |