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filingDate 2015-08-19-04:00^^<http://www.w3.org/2001/XMLSchema#date>
grantDate 2021-07-09-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_1bbc772532db2ce3a17bf7abeb60e459
publicationDate 2021-07-09-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber ES-2841745-T3
titleOfInvention Treatment of glycosylation deficiency diseases
abstract A uridine prodrug for use in treating a genetic disorder of glycosylation in a subject, wherein said treatment comprises administering the uridine prodrug to the subject in an amount sufficient to raise the subject's plasma uridine to a higher level than 30 micromolar; wherein the uridine prodrug is uridine triacetate; and wherein: (a) said treatment comprises administering the uridine prodrug in one or more doses of 0.5 to 5 grams of the uridine prodrug per square meter of body surface area; wherein optionally the uridine prodrug dose is 1.5 to 3 grams per meter of body surface area; (b) the uridine prodrug is formulated for administration in one or more doses of 0.5 to 5 grams of the uridine prodrug per square meter of body surface area; wherein optionally the uridine prodrug dose is 1.5 to 3 grams per meter of body surface area; or (c) said treatment comprises the administration of the uridine prodrug in one or more doses of 2 to 10 grams.
priorityDate 2014-08-19-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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