http://rdf.ncbi.nlm.nih.gov/pubchem/patent/ES-2745470-T3

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assignee http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_f07ba5e7ff356b7eda43fdfc20eef4b0
classificationCPCAdditional http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2799-025
classificationCPCInventive http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K48-0075
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-86
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classificationIPCInventive http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K48-00
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N9-48
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-86
filingDate 2012-04-02-04:00^^<http://www.w3.org/2001/XMLSchema#date>
grantDate 2020-03-02-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_e116e8eadec06d02e27f678e3631efd4
publicationDate 2020-03-02-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber ES-2745470-T3
titleOfInvention AAV2 particle comprising a AAV2 capsid protein and a vector comprising a nucleic acid encoding a tripeptidyl peptidase 1 (TPP1) for the treatment of late childhood ceroid lipofuscinosis (LINCL) in a non-rodent mammal by intraventricular injection or administration icv
abstract An AAVr2 particle comprising an AAV2 capsid protein and a vector comprising a nucleic acid encoding a therapeutic protein inserted between a pair of AAV inverted terminal repeats for use in treating lysosomal storage disease (LSD) in a non-rodent mammal, wherein said AAVr2 particle will be administered to the non-rodent mammal by intraventricular injection or ICV administration, wherein the protein is tripeptidyl peptidase 1 (TPP1), wherein LSD is late infantile ceroid lipofuscinosis (LINCL) and wherein the non-rodent mammal is a dog, primate, or human.
priorityDate 2011-03-31-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID231
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Total number of triples: 939.