http://rdf.ncbi.nlm.nih.gov/pubchem/patent/ES-2745470-T3
Outgoing Links
Predicate | Object |
---|---|
assignee | http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_f07ba5e7ff356b7eda43fdfc20eef4b0 |
classificationCPCAdditional | http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2799-025 |
classificationCPCInventive | http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K48-0075 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-86 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N9-485 |
classificationIPCInventive | http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K48-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N9-48 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-86 |
filingDate | 2012-04-02-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
grantDate | 2020-03-02-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
inventor | http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_e116e8eadec06d02e27f678e3631efd4 |
publicationDate | 2020-03-02-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
publicationNumber | ES-2745470-T3 |
titleOfInvention | AAV2 particle comprising a AAV2 capsid protein and a vector comprising a nucleic acid encoding a tripeptidyl peptidase 1 (TPP1) for the treatment of late childhood ceroid lipofuscinosis (LINCL) in a non-rodent mammal by intraventricular injection or administration icv |
abstract | An AAVr2 particle comprising an AAV2 capsid protein and a vector comprising a nucleic acid encoding a therapeutic protein inserted between a pair of AAV inverted terminal repeats for use in treating lysosomal storage disease (LSD) in a non-rodent mammal, wherein said AAVr2 particle will be administered to the non-rodent mammal by intraventricular injection or ICV administration, wherein the protein is tripeptidyl peptidase 1 (TPP1), wherein LSD is late infantile ceroid lipofuscinosis (LINCL) and wherein the non-rodent mammal is a dog, primate, or human. |
priorityDate | 2011-03-31-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
type | http://data.epo.org/linked-data/def/patent/Publication |
Incoming Links
Total number of triples: 939.