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filingDate 2013-04-23-04:00^^<http://www.w3.org/2001/XMLSchema#date>
grantDate 2017-10-25-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2017-10-25-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber ES-2639066-T3
titleOfInvention RNA modulation oligonucleotides with improved characteristics for the treatment of neuromuscular disorders
abstract Oligonucleotide consisting of nucleotide residues of 2'-O-methyl RNA with a skeleton where all phosphate fractions are replaced by phosphorothioate fractions, said oligonucleotide with a base sequence consisting of (XYG) 7 where each X is 5 -methylcytosine and each Y is uracil (SEQ ID NO: 90).
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Total number of triples: 575.