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grantDate 2016-03-07-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2016-03-07-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber ES-2562658-T3
titleOfInvention Procedures and means for efficient skipping of exon 45 in the pre-mRNA of Duchenne muscular dystrophy
abstract An antisense oligonucleotide, wherein said antisense oligonucleotide is capable of binding to a stretch of at least 21 nucleotides within the following nucleotide sequence within exon 45 of the dystrophin pre-mRNA: ** Formula ** and wherein said oligonucleotide has a length of at least 21 nucleotides and in which said antisense oligonucleotide does not consist of 5'-AACAGTTTGCCGCTGCCAATGCCA-3 ', 5'-CTGACAACAGTTTGCCGCTGCCCAA-3', 5'-GTTGCATTCAATGTTCTGACAAGAG-CTTCCTCCTCCTGT-3GCCAACAG-TTCTGACAACAGT-3GCCAACAGT-3 or 5'-ATTATTTCTTCCCCAGTTGCATTCA-3 '.
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